Fabry Disease: Clinical Trials

1 trial for Fabry Disease, newest first

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1 withdrawn. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Withdrawn 1
Phase 21Withdrawn 1

Follow Fabry Disease: new trials by email Literature Review of Fabry Disease trials Research Report on Fabry Disease

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety and Effect of Oral RVX000222 in Subjects With Fabry Disease
RVX000222 - Fabry Disease
Phase 1 / Phase 2WithdrawnResverlogix Corp2022-11-222023-11-18

Narrower conditions

Cardiovascular Diseases (1)  ·  Kidney Diseases (1)

Broader conditions

Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Cerebral Small Vessel Diseases (1)  ·  Cerebrovascular Disorders (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Female Urogenital Diseases (1)  ·  Female Urogenital Diseases and Pregnancy Complications (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Lipidoses (1)  ·  Lysosomal Storage Diseases (1)

Interventions

apabetalone (1)

Sponsors

Resverlogix Corp (1)

Countries

Canada (1)

Top investigators

Michael West, MD (1)