3 recruiting, 2 active not recruiting. 5 Early Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Early Phase 1 | 5 | Recruiting 3, Active not recruiting 2 |
Follow Duchenne Muscular Dystrophy (DMD): new trials by email Literature Review of Duchenne Muscular Dystrophy (DMD) trials Research Report on Duchenne Muscular Dystrophy (DMD)
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study to Evaluate the Safety and Tolerability of RAG-18 in Pediatric Patients With Duchenne Muscular Dystrophy RAG-18 - Duchenne Muscular Dystrophy (DMD) | Early Phase 1 | Active not recruiting | Peking Union Medical College Hospital | 12 | 2025-12-12 | 2026-01-16 |
| Safety and Dystrophin Expression of SPOT-03 in Duchenne Muscular Dystrophy (DMD) Patients SPOT-03 - Duchenne Muscular Dystrophy (DMD) | Early Phase 1 | Recruiting | Shanghai Siponuoyin Biotechnology Co Ltd | 9 | 2025-08-06 | 2026-05-07 |
| Evaluation of the Safety, Tolerability, and Efficacy of LE051 in Patients With Duchenne Muscular Dystrophy LE051 - Duchenne Muscular Dystrophy (DMD) | Early Phase 1 | Recruiting | Shanghai Jiao Tong University School of Medicine | 12 | 2024-10-24 | 2025-04-02 |
| Evaluation of the Safety and Efficacy of BBM-D101 to Treat Patients with Duchenne Muscular Dystrophy BBM-D101 - Duchenne Muscular Dystrophy (DMD) | Early Phase 1 | Recruiting | Shanghai Jiao Tong University School of Medicine | 6 | 2024-07-25 | 2025-03-25 |
| A Study to Evaluate the Safety and Tolerability of GEN6050X in Duchenne Muscular Dystrophy. GEN6050X intravenous injection - Duchenne Muscular Dystrophy (DMD) | Early Phase 1 | Active not recruiting | Peking Union Medical College Hospital | 3 | 2024-07-05 | 2025-07-29 |
Muscular Dystrophy, Duchenne (5) · Muscular Dystrophies (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5) · Genetic Diseases, Inborn (5) · Genetic Diseases, X-Linked (5) · Muscular Diseases (5) · Muscular Disorders, Atrophic (5) · Musculoskeletal Diseases (5) · Nervous System Diseases (5) · Neuromuscular Diseases (5) · Muscular Dystrophies (4)
Peking Union Medical College Hospital (2) · Shanghai Jiao Tong University School of Medicine (2) · Shanghai Siponuoyin Biotechnology Co Ltd (1)
China (5)
Jiwen Wang (1) · Wang Jiwen (1)