3 active not recruiting. 3 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 3 | Active not recruiting 3 |
Follow DMD: new trials by email Literature Review of DMD trials Research Report on DMD
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients SAT-3247, Placebo - Duchenne Muscular Dystrophy, Duchenne | Phase 2 | Active not recruiting | Satellos Bioscience, Inc. | 51 | 2025-12-08 | 2026-10-02 |
| NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD) NS-089/NCNP-02 - Duchenne Muscular Dystrophy, Exon 44 | Phase 2 | Active not recruiting | NS Pharma, Inc. | 20 | 2024-02-22 | 2026-09-15 |
| Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 Skipping AOC 1044 - DMD, Duchenne Muscular Dystrophy | Phase 2 | Active not recruiting | Avidity Biosciences, Inc. | 39 | 2024-01-22 | 2026-07-30 |
Muscular Dystrophy, Duchenne (3) · Muscular Dystrophies (1) · Neuromuscular Diseases (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Genetic Diseases, Inborn (3) · Genetic Diseases, X-Linked (3) · Muscular Diseases (3) · Muscular Disorders, Atrophic (3) · Musculoskeletal Diseases (3) · Nervous System Diseases (3) · Muscular Dystrophies (2) · Neuromuscular Diseases (2)
Avidity Biosciences, Inc. (1) · NS Pharma, Inc. (1) · Satellos Bioscience, Inc. (1)
United States (3) · Australia (2) · Canada (2) · Belgium (1) · Japan (1) · New Zealand (1) · Poland (1) · Serbia (1) · South Korea (1) · Spain (1) · Turkey (Türkiye) (1) · United Kingdom (1)
2025 (1)