DMD: Clinical Trials

3 trials for DMD, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

3 active not recruiting. 3 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 23Active not recruiting 3

Follow DMD: new trials by email Literature Review of DMD trials Research Report on DMD

Trials (filtered) newest first · largest first

All 3 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients
SAT-3247, Placebo - Duchenne Muscular Dystrophy, Duchenne
Phase 2Active not recruitingSatellos Bioscience, Inc.512025-12-082026-10-02
NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)
NS-089/NCNP-02 - Duchenne Muscular Dystrophy, Exon 44
Phase 2Active not recruitingNS Pharma, Inc.202024-02-222026-09-15
Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 Skipping
AOC 1044 - DMD, Duchenne Muscular Dystrophy
Phase 2Active not recruitingAvidity Biosciences, Inc.392024-01-222026-07-30

Narrower conditions

Muscular Dystrophy, Duchenne (3)  ·  Muscular Dystrophies (1)  ·  Neuromuscular Diseases (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Genetic Diseases, Inborn (3)  ·  Genetic Diseases, X-Linked (3)  ·  Muscular Diseases (3)  ·  Muscular Disorders, Atrophic (3)  ·  Musculoskeletal Diseases (3)  ·  Nervous System Diseases (3)  ·  Muscular Dystrophies (2)  ·  Neuromuscular Diseases (2)

Sponsors

Avidity Biosciences, Inc. (1)  ·  NS Pharma, Inc. (1)  ·  Satellos Bioscience, Inc. (1)

Countries

United States (3)  ·  Australia (2)  ·  Canada (2)  ·  Belgium (1)  ·  Japan (1)  ·  New Zealand (1)  ·  Poland (1)  ·  Serbia (1)  ·  South Korea (1)  ·  Spain (1)  ·  Turkey (Türkiye) (1)  ·  United Kingdom (1)

Top investigators

Carmen Castrillo, MD (1)

NIH funding

2025 (1)