1 completed. 1 Phase 2, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Completed 1 |
| Phase 3 | 1 | Completed 1 |
Follow Classic Galactosemia: new trials by email Literature Review of Classic Galactosemia trials Research Report on Classic Galactosemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Clinical Benefit, Safety, PK and PD Study of AT-007 in Pediatric Subjects With Classic Galactosemia AT-007, Placebo - Classic Galactosemia | Phase 2 / Phase 3 | Completed | Applied Therapeutics, Inc. | 47 | 2021-03-20 | 2025-10-29 |
Galactosemias (1)
Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Carbohydrate Metabolism, Inborn Errors (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Nervous System Diseases (1) · Nutritional and Metabolic Diseases (1)
Applied Therapeutics, Inc. (1)
United States (1)
Jonathan W Mink, MD (1) · Susan E Waisbren, PhD (1)