1 completed. .
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| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Farber Disease Natural History Study Farber Disease, Farber's Disease | Completed | Sumitomo Pharma Switzerland GmbH | 45 | 2017-11-22 | 2020-01-18 |
Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Connective Tissue Diseases (1) · Farber Lipogranulomatosis (1) · Genetic Diseases, Inborn (1) · Infant, Newborn, Diseases (1) · Lipid Metabolism Disorders (1) · Lipidoses (1) · Lysosomal Storage Diseases (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Musculoskeletal Diseases (1) · Neurologic Manifestations (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Lipid Metabolism, Inborn Errors (1) · Lysosomal Storage Diseases, Nervous System (1) · Nervous System Diseases (1) · Nutritional and Metabolic Diseases (1) · Pathological Conditions, Signs and Symptoms (1) · Signs and Symptoms (1) · Skin and Connective Tissue Diseases (1)
Sumitomo Pharma Switzerland GmbH (1)
Argentina (1) · Canada (1) · Egypt (1) · Germany (1) · India (1) · Italy (1) · Sweden (1) · Turkey (Türkiye) (1) · United States (1)