PBA: Clinical Trials

3 trials of PBA, newest first

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2 completed, 1 suspended. 1 Early Phase 1, 1 Not applicable, 1 Phase 1.

By phase and status

PhaseTrialsStatus
Early Phase 11Suspended 1
Not applicable1Completed 1
Phase 11Completed 1

Follow PBA: new trials by email Literature Review of PBA trials Research Report on PBA

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
PBA Use for Treatment of ATF6-/- Patients
PBA - ACHROMATOPSIA 7, Achromatopsia
Early Phase 1SuspendedColumbia University22025-04-082026-09-11
Safety and Tolerability of Phenylbutyrate in Inclusion Body Myositis
Phenylbutyrate Oral Tablet - Inclusion Body Myositis, Sporadic Inclusion Body Myositis
Phase 1CompletedUniversity of Kansas Medical Center102020-08-202024-09-19
Effect of Endoplasmic Reticulum Stress on Metabolic Function
tauroursodeoxycholic acid, placebo, sodium phenylbutyrate - Insulin Resistance, Diabetes
Not applicableCompletedWashington University School of Medicine1012008-02-012018-05-29

Conditions studied

Color Vision Defects (1)  ·  Diabetes Mellitus (1)  ·  Diabetes Mellitus, Type 2 (1)  ·  Insulin Resistance (1)  ·  Myositis, Inclusion Body (1)  ·  Obesity (1)

Sponsors

Columbia University (1)  ·  University of Kansas Medical Center (1)  ·  Washington University School of Medicine (1)

Countries

United States (3)

Top investigators

Duaa Jabari, MD (1)  ·  Samuel Klein, MD (1)  ·  Stephen Tsang, MD (1)

Results publications

PMID 20522594