1 suspended. 1 Early Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Early Phase 1 | 1 | Suspended 1 |
Follow PBA: new trials by email Literature Review of PBA trials Research Report on PBA
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| PBA Use for Treatment of ATF6-/- Patients PBA - ACHROMATOPSIA 7, Achromatopsia | Early Phase 1 | Suspended | Columbia University | 2 | 2025-04-08 | 2026-09-11 |
United States (1)