fitusiran: Clinical Trials

2 trials of fitusiran, newest first

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2 completed. 2 Phase 2, 1 Phase 1, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 22Completed 2
Phase 11Completed 1
Phase 31Completed 1

Follow fitusiran: new trials by email Literature Review of fitusiran trials Research Report on fitusiran

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Fitusiran Prophylaxis in Male Pediatric Subjects Aged 1 to Less Than 12 Years With Hemophilia A or B
Fitusiran - Hemophilia
Phase 2 / Phase 3CompletedGenzyme, a Sanofi Company322020-01-282026-09-28
An Open-label Extension Study of an Investigational Drug, Fitusiran, in Patients With Moderate or Severe Hemophilia A or B
Fitusiran (SAR439774) - Hemophilia A, Hemophilia B
Phase 1 / Phase 2CompletedGenzyme, a Sanofi Company342015-09-182024-06-05

Conditions studied

Hemophilia A (2)  ·  Hemophilia B (1)

Sponsors

Genzyme, a Sanofi Company (2)

Countries

United States (2)  ·  Bulgaria (1)  ·  Canada (1)  ·  India (1)  ·  Italy (1)  ·  Russia (1)  ·  Spain (1)  ·  Switzerland (1)  ·  Turkey (Türkiye) (1)  ·  United Kingdom (1)

Results publications

PMID 39642315

NIH funding

2015 (1), 2019 (1)