deflazacort: Clinical Trials

5 trials of deflazacort, newest first

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2 completed, 1 active not recruiting, 1 terminated, 1 withdrawn. 5 Phase 3, 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 35Completed 2, Active not recruiting 1, Terminated 1, Withdrawn 1
Phase 22Active not recruiting 1, Completed 1

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Trials (filtered) newest first · largest first

All 5 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Deflazacort Vs. Prednisolone in Acute-stage ABPA
Deflazacort, Prednisolone - Allergic Bronchopulmonary Aspergillosis
Phase 2 / Phase 3Active not recruitingPost Graduate Institute of Medical Education and Research, Chandigarh1502020-01-152025-02-28
A Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle Muscular Dystrophy 2I (LGMD2I)
Deflazacort - Limb-Girdle Muscular Dystrophy
Phase 3TerminatedPTC Therapeutics112019-10-312022-06-27
A Study of Deflazacort (Emflaza®) in Participants With Duchenne Muscular Dystrophy (DMD)
Deflazacort - Duchenne Muscular Dystrophy
Phase 3WithdrawnPTC Therapeutics2018-10-312019-06-21
Finding the Optimum Regimen for Duchenne Muscular Dystrophy
Prednisone, Deflazacort - Duchenne Muscular Dystrophy
Phase 3CompletedUniversity of Rochester1962013-01-012022-08-12
Deflazacort in Dysferlinopathies
deflazacort, placebo - LGMD2B, Miyoshi Myopathy
Phase 2 / Phase 3CompletedLudwig-Maximilians - University of Munich252003-09-012015-09-02

Conditions studied

Muscular Dystrophies (2)  ·  Muscular Dystrophy, Duchenne (2)  ·  Aspergillosis, Allergic Bronchopulmonary (1)  ·  Asthma (1)  ·  Dysferlinopathy (1)  ·  Limb-girdle muscular dystrophy, type 2B (1)  ·  Miyoshi myopathy (1)  ·  Muscular Dystrophies, Limb-Girdle (1)  ·  Neuromuscular Diseases (1)

Sponsors

PTC Therapeutics (2)  ·  Ludwig-Maximilians - University of Munich (1)  ·  Post Graduate Institute of Medical Education and Research, Chandigarh (1)  ·  University of Rochester (1)

Countries

Germany (3)  ·  Canada (2)  ·  United States (2)  ·  Denmark (1)  ·  France (1)  ·  India (1)  ·  Italy (1)  ·  Norway (1)  ·  Russia (1)  ·  Sweden (1)  ·  United Kingdom (1)

Top investigators

Cristobal Passalacqua, MD (1)  ·  Francesco Bibbiani, MD (1)  ·  Kate Bushby, MD (1)  ·  Maggie C. Walter, MD (1)  ·  Robert C. Griggs, MD (1)

Results publications

PMID 23406536, PMID 34857536, PMID 35381069, PMID 42139655, PMID 42202243, PMID 42249273, PMID 42443978

NIH funding

U01NS061799 (1)