Tuberous Sclerosis: Clinical Trials

2 trials for Tuberous Sclerosis, newest first

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2 terminated. 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 22Terminated 2

Follow Tuberous Sclerosis: new trials by email Literature Review of Tuberous Sclerosis trials Research Report on Tuberous Sclerosis

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Topical Sirolimus Ointment for Cutaneous Angiofibromas in Subjects With Tuberous Sclerosis Complex
Sirolimus 0.2%, Sirolimus 0.4%, Placebo ointment - Angiofibroma of Face, Tuberous Sclerosis
Phase 2TerminatedAucta Pharmaceuticals, Inc242017-04-122025-12-01
Treatment of Renal Angiomyolipomas in Tuberous Sclerosis by Beta-blockers
Propranolol - Renal Angiomyolipomas, Tuberous Sclerosis
Phase 2TerminatedUniversity Hospital, Bordeaux22015-05-222026-06-24

Narrower conditions

Erythema (1)  ·  Exanthema (1)  ·  Facies (1)  ·  Fibroma (1)

Broader conditions

Congenital Abnormalities (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Hamartoma (2)  ·  Heredodegenerative Disorders, Nervous System (2)  ·  Malformations of Cortical Development (2)  ·  Malformations of Cortical Development, Group I (2)  ·  Neoplasms (2)  ·  Neoplasms, Multiple Primary (2)  ·  Neoplastic Syndromes, Hereditary (2)  ·  Nervous System Diseases (2)  ·  Nervous System Malformations (2)  ·  Neurocutaneous Syndromes (2)  ·  Neurodegenerative Diseases (2)  ·  Disease Attributes (1)

Interventions

Propranolol (1)  ·  Sirolimus (1)

Sponsors

Aucta Pharmaceuticals, Inc (1)  ·  University Hospital, Bordeaux (1)

Countries

China (1)  ·  France (1)  ·  United States (1)

Top investigators

Shoufeng Li, Ph.D (1)