Thalassemia: Clinical Trials

1 trial for Thalassemia, newest first

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1 enrolling by invitation. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Enrolling by invitation 1

Follow Thalassemia: new trials by email Literature Review of Thalassemia trials Research Report on Thalassemia

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Long-term Follow-up Study in Participants Who Received CTX001
CTX001 - Beta-Thalassemia, Thalassemia
Phase 3Enrolling by invitationVertex Pharmaceuticals Incorporated1602021-01-202026-08-11

Narrower conditions

Anemia, Sickle Cell (1)  ·  Genetic Diseases, Inborn (1)  ·  Hematologic Diseases (1)  ·  Hemoglobinopathies (1)  ·  beta-Thalassemia (1)

Broader conditions

Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Hemolytic, Congenital (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Hemic and Lymphatic Diseases (1)

Interventions

exagamglogene autotemcel (1)

Sponsors

Vertex Pharmaceuticals Incorporated (1)

Countries

Belgium (1)  ·  Canada (1)  ·  Germany (1)  ·  Italy (1)  ·  United Kingdom (1)  ·  United States (1)

Results publications

PMID 40857358, PMID 40862696, PMID 42252696