Stargardt Disease: Clinical Trials

2 trials for Stargardt Disease, newest first

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2 completed. 2 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 32Completed 2

Follow Stargardt Disease: new trials by email Literature Review of Stargardt Disease trials Research Report on Stargardt Disease

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase 3, Randomized, Placebo-Controlled Study of Tinlarebant to Explore Safety and Efficacy in Adolescent Stargardt Disease
Tinlarebant, Placebo - Stargardt Disease 1
Phase 3CompletedBelite Bio, Inc1042022-03-282026-07-23
Safety and Efficacy of Emixustat in Stargardt Disease
Emixustat, Placebo - Stargardt Disease
Phase 3CompletedKubota Vision Inc.1942019-01-072024-05-30

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Eye Diseases (2)  ·  Eye Diseases, Hereditary (2)  ·  Genetic Diseases, Inborn (2)  ·  Macular Degeneration (2)  ·  Retinal Degeneration (2)  ·  Retinal Diseases (2)

Interventions

emixustat (1)

Sponsors

Belite Bio, Inc (1)  ·  Kubota Vision Inc. (1)

Countries

France (2)  ·  Germany (2)  ·  Netherlands (2)  ·  United Kingdom (2)  ·  United States (2)  ·  Australia (1)  ·  Belgium (1)  ·  Brazil (1)  ·  Canada (1)  ·  China (1)  ·  Denmark (1)  ·  Hong Kong (1)  ·  Italy (1)  ·  South Africa (1)  ·  Spain (1)

Top investigators

Jeff Gregory, MD (1)