Rett Syndrome: Clinical Trials

3 trials for Rett Syndrome, newest first

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3 completed. 3 Phase 1, 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 13Completed 3
Phase 22Completed 2

Follow Rett Syndrome: new trials by email Literature Review of Rett Syndrome trials Research Report on Rett Syndrome

Trials (filtered) newest first · largest first

All 3 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Assessing the Safety and Efficacy of Full-Spectrum Medicinal Cannabis Plant Extract 0.08% THC (NTI164) in the Treatment of Rett Syndrome (RTT)
NTI164 - Rett Syndrome
Phase 1 / Phase 2CompletedFenix Innovation Group142023-09-202026-09-09
Study to Assess Safety and Efficacy of Fingolimod in Children With Rett Syndrome
fingolimod (FTY720) - Rett's Syndrome
Phase 1 / Phase 2CompletedUniversity Hospital, Basel, Switzerland62013-08-012018-06-15
Treatment of Rett Syndrome With rhIGF-1 (Mecasermin [rDNA]Injection)
rhIGF-1 - Rett Syndrome
Phase 1CompletedBoston Children's Hospital122010-12-012017-06-22

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Genetic Diseases, Inborn (3)  ·  Genetic Diseases, X-Linked (3)  ·  Heredodegenerative Disorders, Nervous System (3)  ·  Intellectual Disability (3)  ·  Nervous System Diseases (3)  ·  Neurobehavioral Manifestations (3)  ·  Neurologic Manifestations (3)  ·  X-Linked Intellectual Disability (3)

Interventions

Fingolimod Hydrochloride (1)  ·  mecasermin (1)

Sponsors

Boston Children's Hospital (1)  ·  Fenix Innovation Group (1)  ·  University Hospital, Basel, Switzerland (1)

Countries

Australia (1)  ·  Switzerland (1)  ·  United States (1)

Top investigators

Ludwig Kappos, Prof. (1)  ·  Mustafa Sahin, MD, PhD (1)

Results publications

PMID 33407685