1 completed. 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Completed 1 |
Follow Retinopathy: new trials by email Literature Review of Retinopathy trials Research Report on Retinopathy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| EPI-743 in Cobalamin C Defect: Effects on Visual and Neurological Impairment Epi-743, Placebo supplementation - Methylmalonic Aciduria and Homocystinuria,Cblc Type, Genetic Disease | Phase 2 | Completed | Bambino Gesù Hospital and Research Institute | 30 | 2013-01-01 | 2017-04-25 |
Genetic Diseases, Inborn (1) · Methylmalonic acidemia with homocystinuria (1) · Retinal Diseases (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Eye Diseases (1)
Bambino Gesù Hospital and Research Institute (1)
Italy (1)
Carlo Dionisi-Vici, MD (1) · Daniela Ricci, MD,PhD (1) · Diego Martinelli, MD, PhD (1) · Giancarlo Iarossi, MD (1)