2 active not recruiting, 1 completed. 2 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Active not recruiting 1, Completed 1 |
| Phase 2 | 1 | Active not recruiting 1 |
Follow Retinitis Pigmentosa 11: new trials by email Literature Review of Retinitis Pigmentosa 11 trials Research Report on Retinitis Pigmentosa 11
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Repeat-Dose, Open-Label, Two Arm Safety and Efficacy Study of Two Doses of VP-001 Administered Intravitreally in Participants With Confirmed PRPF31 Mutation-Associated Retinal Dystrophy, Including Participants Previously Treated With VP001 VP-001 - Retinitis Pigmentosa 11, Retinal Degeneration | Phase 1 / Phase 2 | Active not recruiting | PYC Therapeutics | 17 | 2025-06-01 | 2026-05-29 |
| MAD of IVT VP-001 in PRPF31 Mutation-Associated Retinal Dystrophy Subjects (Wallaby) VP-001 - Retinitis Pigmentosa 11, Retinal Degeneration | Phase 1 | Completed | PYC Therapeutics | 6 | 2024-06-13 | 2026-05-29 |
| Natural History Study of Retinitis Pigmentosa Type 11 Clinical examinations - Retinitis Pigmentosa 11, Retinitis Pigmentosa | Active not recruiting | Oslo University Hospital | 30 | 2021-02-01 | 2025-03-21 |
Retinal Degeneration (2) · Retinal Diseases (2) · Retinal Dystrophies (2) · Eye Diseases (1) · Eye Diseases, Hereditary (1) · Retinitis (1) · Retinitis Pigmentosa (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Eye Diseases (2) · Eye Diseases, Hereditary (2) · Genetic Diseases, Inborn (2) · Retinal Degeneration (1) · Retinal Diseases (1) · Retinal Dystrophies (1)
PYC Therapeutics (2) · Oslo University Hospital (1)
United States (2) · Norway (1)