1 active not recruiting. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Active not recruiting 1 |
| Phase 2 | 1 | Active not recruiting 1 |
Follow Pompe Disease: new trials by email Literature Review of Pompe Disease trials Research Report on Pompe Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE) SPK-3006 - Pompe Disease, Pompe Disease (Late-onset) | Phase 1 / Phase 2 | Active not recruiting | Spark Therapeutics, Inc. | 4 | 2020-10-01 | 2024-11-27 |
Glycogen Storage Disease Type II (1) · Lysosomal Storage Diseases (1)
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