2 completed, 1 enrolling by invitation. 3 Phase 2, 2 Phase 1, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 3 | Completed 2, Enrolling by invitation 1 |
| Phase 1 | 2 | Completed 1, Enrolling by invitation 1 |
| Phase 3 | 1 | Completed 1 |
Follow Myelokathexis: new trials by email Literature Review of Myelokathexis trials Research Report on Myelokathexis
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Base-Edited Hematopoietic Stem/Progenitor Cell Gene Therapy for Treatment of CXCR4-WHIM Busulfan, Palifermin, Plerixafor - WHIM, Warts | Phase 1 / Phase 2 | Enrolling by invitation | National Institute of Allergy and Infectious Diseases (NIAID) | 10 | 2026-10-21 | 2026-10-27 |
| Plerixafor Versus G-CSF in the Treatment of People With WHIM Syndrome Plerixafor, G-CSF - Myelokathexis, Infections | Phase 2 / Phase 3 | Completed | National Institute of Allergy and Infectious Diseases (NIAID) | 20 | 2014-10-14 | 2026-06-26 |
| A Phase I Study of Mozobil in the Treatment of Patients With WHIMS Mozobil (TM) - Leukopenia, Neutropenia | Phase 1 / Phase 2 | Completed | National Institute of Allergy and Infectious Diseases (NIAID) | 14 | 2010-01-06 | 2026-09-28 |
Agammaglobulinemia (3) · Immunologic Deficiency Syndromes (3) · Warts (3) · Infections (2) · Neutropenia (2) · Leukopenia (1)
Blood Protein Disorders (3) · DNA Virus Infections (3) · Hematologic Diseases (3) · Hemic and Lymphatic Diseases (3) · Immune System Diseases (3) · Lymphatic Diseases (3) · Lymphoproliferative Disorders (3) · Papillomavirus Infections (3) · Skin Diseases (3) · Skin Diseases, Infectious (3) · Skin Diseases, Viral (3) · Skin and Connective Tissue Diseases (3) · Tumor Virus Infections (3) · Virus Diseases (3) · Agranulocytosis (2)
plerixafor (3) · Filgrastim (2) · Busulfan (1) · Fibroblast Growth Factor 7 (1) · Granulocyte Colony-Stimulating Factor (1)
National Institute of Allergy and Infectious Diseases (NIAID) (3)
United States (3)
David H McDermott, M.D. (2) · Suk S De Ravin, M.D. (1)
PMID 21890643, PMID 24523241, PMID 24723677, PMID 37561579, PMID 40330596, PMID 42606118