Myasthenia Gravis, MuSK: Clinical Trials

4 trials for Myasthenia Gravis, MuSK, newest first

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3 recruiting, 1 terminated. 1 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 21Recruiting 1
Phase 31Terminated 1

Follow Myasthenia Gravis, MuSK: new trials by email Literature Review of Myasthenia Gravis, MuSK trials Research Report on Myasthenia Gravis, MuSK

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
AXIS MG Patient Registry
Myasthenia Gravis (MG), Myasthenia Gravis, Generalized
RecruitingAutoimmune Neurology Alliance10002026-03-192026-08-17
Safety and Efficacy of 3 Dose Levels of NMD670 in Adult Patients With Myasthenia Gravis
NMD670, Placebo - Myasthenia Gravis, Myasthenia Gravis, MuSK
Phase 2RecruitingNMD Pharma A/S842024-05-162026-08-21
Long Term Safety Study of Amifampridine Phosphate in MuSK-MG (Muscle Specific Tyrosine Kinase Myasthenia Gravis)
Amifampridine Phosphate - Myasthenia Gravis, MuSK, AChR Myasthenia Gravis
Phase 3TerminatedCatalyst Pharmaceuticals, Inc.632018-06-112024-05-07
Myasthenia Gravis Foundation of America Global MG Patient Registry
Myasthaenia Gravis, Myasthenia
RecruitingMyasthenia Gravis Foundation of America38002013-10-122024-09-27

Narrower conditions

Myasthenia Gravis (4)  ·  Autoimmune Diseases of the Nervous System (1)  ·  Disease Progression (1)  ·  Medication Adherence (1)  ·  Neuromuscular Junction Diseases (1)

Broader conditions

Autoimmune Diseases (4)  ·  Immune System Diseases (4)  ·  Neoplasms (4)  ·  Neoplasms by Site (4)  ·  Nervous System Diseases (4)  ·  Nervous System Neoplasms (4)  ·  Neurodegenerative Diseases (4)  ·  Neuromuscular Diseases (4)  ·  Paraneoplastic Syndromes (4)  ·  Paraneoplastic Syndromes, Nervous System (4)  ·  Autoimmune Diseases of the Nervous System (3)  ·  Neuromuscular Junction Diseases (3)  ·  Behavior (1)  ·  Disease Attributes (1)  ·  Health Behavior (1)

Interventions

Amifampridine (1)

Sponsors

Autoimmune Neurology Alliance (1)  ·  Catalyst Pharmaceuticals, Inc. (1)  ·  Myasthenia Gravis Foundation of America (1)  ·  NMD Pharma A/S (1)

Countries

United States (4)  ·  Italy (2)  ·  Belgium (1)  ·  Denmark (1)  ·  France (1)  ·  Georgia (1)  ·  Netherlands (1)  ·  Poland (1)  ·  Serbia (1)  ·  Spain (1)

Top investigators

Gary R Cutter, PhD (1)  ·  Jared R Adams, MD, PhD (1)  ·  Neelam Goyal, MD (1)  ·  Renato Mantegazza, MD (1)  ·  Richard J Nowak, MD, MS (1)  ·  Srikanth Muppidi, MD (1)

Results publications

PMID 41224659

NIH funding

2023 (1)