1 not yet recruiting, 1 recruiting, 1 terminated. 1 Phase 1, 1 Phase 2, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Terminated 1 |
| Phase 2 | 1 | Terminated 1 |
| Phase 3 | 1 | Recruiting 1 |
Follow Muscular Dystrophy (DMD): new trials by email Literature Review of Muscular Dystrophy (DMD) trials Research Report on Muscular Dystrophy (DMD)
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO) Zeleciment Rostudirsen (DYNE-251), Placebo - Duchenne Muscular Dystrophy (DMD), Muscular Dystrophy, Duchenne | Phase 3 | Recruiting | Dyne Therapeutics | 90 | 2026-06-01 | 2026-05-27 |
| A Multicenter Cohort Study of Duchenne and Becker Muscular Dystrophy in Western Chinese Children No interventions are applied; participants are followed for natural history observation only - Muscular Dystrophy, Becker, Muscular Dystrophy | Not yet recruiting | West China Second University Hospital | 500 | 2026-04-20 | 2026-04-06 | |
| Study of an Investigational Drug, RO7239361 (BMS-986089), in Ambulatory Boys With DMD RO7239361, Placebo - Muscular Dystrophy (DMD) | Phase 1 / Phase 2 | Terminated | Hoffmann-La Roche | 43 | 2015-12-02 | 2020-11-04 |
Muscular Dystrophies (3) · Muscular Dystrophy, Duchenne (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Myotonic Dystrophy (1) · Neuromuscular Diseases (1)
Muscular Diseases (3) · Muscular Disorders, Atrophic (3) · Musculoskeletal Diseases (3) · Nervous System Diseases (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Neuromuscular Diseases (2) · Genetic Diseases, X-Linked (1) · Heredodegenerative Disorders, Nervous System (1) · Myotonic Disorders (1) · Neurodegenerative Diseases (1)
Dyne Therapeutics (1) · Hoffmann-La Roche (1) · West China Second University Hospital (1)
United States (2) · Canada (1) · China (1)
2025 (1)