Muscular Dystrophy, Duchenne Type: Clinical Trials

2 trials for Muscular Dystrophy, Duchenne Type, newest first

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1 completed, 1 recruiting. 1 Not applicable, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Not applicable1Completed 1
Phase 31Recruiting 1

Follow Muscular Dystrophy, Duchenne Type: new trials by email Literature Review of Muscular Dystrophy, Duchenne Type trials Research Report on Muscular Dystrophy, Duchenne Type

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
Zeleciment Rostudirsen (DYNE-251), Placebo - Duchenne Muscular Dystrophy (DMD), Muscular Dystrophy, Duchenne
Phase 3RecruitingDyne Therapeutics902026-06-012026-05-27
Trunk Oriented Exercises Versus Whole-body Vibration for Duchenne Muscular Dystrophy
trunk oriented exercise, whole body vibration - Muscular Dystrophy, Duchenne Type
Not applicableCompletedCairo University302023-01-152023-04-18

Narrower conditions

Muscular Dystrophy, Duchenne (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Muscular Dystrophies (1)  ·  Myotonic Dystrophy (1)  ·  Neuromuscular Diseases (1)

Broader conditions

Muscular Diseases (2)  ·  Muscular Disorders, Atrophic (2)  ·  Musculoskeletal Diseases (2)  ·  Nervous System Diseases (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Muscular Dystrophies (1)  ·  Myotonic Disorders (1)  ·  Neurodegenerative Diseases (1)  ·  Neuromuscular Diseases (1)

Sponsors

Cairo University (1)  ·  Dyne Therapeutics (1)

Countries

Egypt (1)  ·  United States (1)

Results publications

PMID 38427368

NIH funding

2025 (1)