1 completed, 1 recruiting. .
Follow MPS IV: new trials by email Literature Review of MPS IV trials Research Report on MPS IV
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Ultrasound Findings of Finger, Wrist and Knee Joints in Mucopolysaccharidosis MPS I, MPS IV | Completed | Children's Hospital of Eastern Ontario | 18 | 2013-09-01 | 2018-01-24 | |
| Longitudinal Study of Neurodegenerative Disorders Palliative Care, Hematopoetic Stem Cell Transplantation - MLD, Krabbe Disease | Recruiting | University of Pittsburgh | 1500 | 2012-01-11 | 2026-02-09 |
Mucopolysaccharidosis IV (2) · Gaucher Disease (1) · Hypermethioninemia (1) · Language (1) · Leukodystrophy, Globoid Cell (1) · Leukoencephalopathies (1) · Lysosomal Storage Diseases (1) · Mucopolysaccharidosis III (1) · Multiple Sulfatase Deficiency Disease (1) · Neuronal Ceroid-Lipofuscinoses (1) · Niemann-Pick Diseases (1) · Osteopetrosis (1) · Pelizaeus-Merzbacher Disease (1) · Purine Nucleoside Phosphorylase Deficiency (1) · Sandhoff Disease (1)
Carbohydrate Metabolism, Inborn Errors (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Connective Tissue Diseases (2) · Genetic Diseases, Inborn (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Mucinoses (2) · Mucopolysaccharidoses (2) · Nutritional and Metabolic Diseases (2) · Skin and Connective Tissue Diseases (2) · Behavior (1) · Bone Diseases (1) · Bone Diseases, Developmental (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1)
Palliative Care (1)
Children's Hospital of Eastern Ontario (1) · University of Pittsburgh (1)
Canada (1) · United States (1)