3 completed, 1 recruiting. .
Follow Morquio Disease: new trials by email Literature Review of Morquio Disease trials Research Report on Morquio Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Establishment of Human Cellular Disease Models for Morquio Disease Morquio Disease | Completed | CENTOGENE GmbH Rostock | 40 | 2018-10-26 | 2021-04-09 | |
| Pregnancy With Morquio Syndrome - What Are Patients' Perspectives and Has ERT Changed Them? Interview - Morquio Disease, MPS - Mucopolysaccharidosis | Completed | Emory University | 18 | 2017-05-10 | 2021-01-20 | |
| Psychological Concomitants of Morquio Syndrome (The MAP Study) Morquio Disease, Mucopolysaccharidosis IV | Completed | Nadia Ali, PhD | 20 | 2012-07-01 | 2013-12-04 | |
| Longitudinal Study of Neurodegenerative Disorders Palliative Care, Hematopoetic Stem Cell Transplantation - MLD, Krabbe Disease | Recruiting | University of Pittsburgh | 1500 | 2012-01-11 | 2026-02-09 |
Mucopolysaccharidosis IV (4) · Gaucher Disease (1) · Hypermethioninemia (1) · Language (1) · Leukodystrophy, Globoid Cell (1) · Leukoencephalopathies (1) · Lysosomal Storage Diseases (1) · Mucopolysaccharidoses (1) · Mucopolysaccharidosis III (1) · Multiple Sulfatase Deficiency Disease (1) · Neuronal Ceroid-Lipofuscinoses (1) · Niemann-Pick Diseases (1) · Osteopetrosis (1) · Pelizaeus-Merzbacher Disease (1) · Psychological Well-Being (1)
Carbohydrate Metabolism, Inborn Errors (4) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4) · Connective Tissue Diseases (4) · Genetic Diseases, Inborn (4) · Metabolic Diseases (4) · Metabolism, Inborn Errors (4) · Mucinoses (4) · Nutritional and Metabolic Diseases (4) · Skin and Connective Tissue Diseases (4) · Lysosomal Storage Diseases (3) · Mucopolysaccharidoses (3) · Behavior (2) · Bone Diseases (1) · Bone Diseases, Developmental (1) · Brain Diseases (1)
Interviews as Topic (1) · Palliative Care (1)
CENTOGENE GmbH Rostock (1) · Emory University (1) · Nadia Ali, PhD (1) · University of Pittsburgh (1)
United States (3) · Pakistan (1)
Arndt Rolfs, Prof. Dr. (1) · Nadia Ali, Ph.D. (1)