Limb-Girdle Muscular Dystrophy: Clinical Trials

1 trial for Limb-Girdle Muscular Dystrophy, newest first

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1 terminated. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Terminated 1

Follow Limb-Girdle Muscular Dystrophy: new trials by email Literature Review of Limb-Girdle Muscular Dystrophy trials Research Report on Limb-Girdle Muscular Dystrophy

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle Muscular Dystrophy 2I (LGMD2I)
Deflazacort - Limb-Girdle Muscular Dystrophy
Phase 3TerminatedPTC Therapeutics112019-10-312022-06-27

Narrower conditions

Muscular Dystrophies, Limb-Girdle (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Muscular Diseases (1)  ·  Muscular Disorders, Atrophic (1)  ·  Muscular Dystrophies (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neuromuscular Diseases (1)

Interventions

deflazacort (1)

Sponsors

PTC Therapeutics (1)

Countries

Canada (1)  ·  Denmark (1)  ·  France (1)  ·  Germany (1)  ·  Norway (1)  ·  Russia (1)  ·  Sweden (1)  ·  United States (1)

Top investigators

Cristobal Passalacqua, MD (1)