1 terminated. 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 1 | Terminated 1 |
Follow Limb-Girdle Muscular Dystrophy: new trials by email Literature Review of Limb-Girdle Muscular Dystrophy trials Research Report on Limb-Girdle Muscular Dystrophy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle Muscular Dystrophy 2I (LGMD2I) Deflazacort - Limb-Girdle Muscular Dystrophy | Phase 3 | Terminated | PTC Therapeutics | 11 | 2019-10-31 | 2022-06-27 |
Muscular Dystrophies, Limb-Girdle (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Muscular Diseases (1) · Muscular Disorders, Atrophic (1) · Muscular Dystrophies (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1) · Neuromuscular Diseases (1)
deflazacort (1)
PTC Therapeutics (1)
Canada (1) · Denmark (1) · France (1) · Germany (1) · Norway (1) · Russia (1) · Sweden (1) · United States (1)