1 completed. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
| Phase 2 | 1 | Completed 1 |
Follow Leber's Congenital Amaurosis: new trials by email Literature Review of Leber's Congenital Amaurosis trials Research Report on Leber's Congenital Amaurosis
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Study to Evaluate QR-110 in Leber's Congenital Amaurosis (LCA) Due to the c.2991+1655A>G Mutation (p.Cys998X) in the CEP290 Gene QR-110 - Leber's Congenital Amaurosis | Phase 1 / Phase 2 | Completed | Laboratoires Thea | 11 | 2017-10-16 | 2024-10-15 |
Meckel Syndrome, Type 4 (1) · Optic Atrophy, Hereditary, Leber (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Cranial Nerve Diseases (1) · Eye Diseases (1) · Eye Diseases, Hereditary (1) · Genetic Diseases, Inborn (1) · Heredodegenerative Disorders, Nervous System (1) · Metabolic Diseases (1) · Mitochondrial Diseases (1) · Nervous System Diseases (1) · Neurodegenerative Diseases (1) · Nutritional and Metabolic Diseases (1) · Optic Atrophies, Hereditary (1) · Optic Atrophy (1) · Optic Nerve Diseases (1)
Belgium (1) · United States (1)
PMID 30559420, PMID 31215818, PMID 33795869, PMID 35379979
2017 (1)