2 active not recruiting. 2 Phase 2, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Active not recruiting 2 |
| Phase 3 | 1 | Active not recruiting 1 |
Follow Hunter Syndrome: new trials by email Literature Review of Hunter Syndrome trials Research Report on Hunter Syndrome
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Extension Study of Idursulfase-IT Along With Elaprase in Children and Adults With Hunter Syndrome and Cognitive Impairment Idursulfase-IT, Elaprase - Hunter Syndrome | Phase 2 / Phase 3 | Active not recruiting | Takeda | 6 | 2024-03-05 | 2025-11-06 |
| MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis Stem Cell Transplantation, IMD Preparative Regimen, Osteopetrosis Only Preparative Regimen - Mucopolysaccharidosis Disorders, Hurler Syndrome | Phase 2 | Active not recruiting | Masonic Cancer Center, University of Minnesota | 149 | 2014-07-10 | 2026-01-07 |
Mucopolysaccharidosis II (2) · Alpha-Methylacyl-CoA Racemase Deficiency (1) · Aspartylglucosaminuria (1) · Fucosidosis (1) · Hereditary Diffuse Leukoencephalopathy with Spheroids (1) · Leukodystrophy, Globoid Cell (1) · Leukodystrophy, Metachromatic (1) · Mucopolysaccharidosis I (1) · Mucopolysaccharidosis VI (1) · Mucopolysaccharidosis VII (1) · Osteopetrosis (1) · Peroxisomal ACYL-COA oxidase deficiency (1) · Peroxisomal Disorders (1) · Pseudo-Zellweger syndrome (1) · Refsum Disease, Infantile (1)
Carbohydrate Metabolism, Inborn Errors (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Connective Tissue Diseases (2) · Genetic Diseases, Inborn (2) · Genetic Diseases, X-Linked (2) · Heredodegenerative Disorders, Nervous System (2) · Intellectual Disability (2) · Lysosomal Storage Diseases (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Mucinoses (2) · Mucopolysaccharidoses (2) · Nervous System Diseases (2) · Neurobehavioral Manifestations (2) · Neurologic Manifestations (2)
Regimen B (1) · Stem Cell Transplantation (1) · idursulfase (1)
Masonic Cancer Center, University of Minnesota (1) · Takeda (1)
Canada (1) · France (1) · United States (1)
2023 (1)