Hemoglobin S Disease: Clinical Trials

4 trials for Hemoglobin S Disease, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 completed, 1 recruiting, 1 terminated. 3 Phase 2, 1 Not applicable.

By phase and status

PhaseTrialsStatus
Phase 23Completed 1, Recruiting 1, Terminated 1
Not applicable1Completed 1

Follow Hemoglobin S Disease: new trials by email Literature Review of Hemoglobin S Disease trials Research Report on Hemoglobin S Disease

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Trial to Assess Haploidentical T-depleted Stem Cell Transplantation in Patients With SCD
TCRα/β+ and CD19+ depleted haploidentical stem cell transplantation, Matched sibling donor transplantation - HbS Disease, Hemoglobin S Disease
Phase 2RecruitingUniversity of Regensburg2122021-06-302024-05-13
Evaluation of a Training Program for Homozygous Sickle Cell Disease Patients
Training Program - Sickle Cell Hemoglobin C Disease, Hemoglobin S Disease
Not applicableCompletedCentre Hospitalier Universitaire de Saint Etienne402014-09-012021-09-13
Effects of HQK-1001 in Patients With Sickle Cell Disease
HQK-1001, Placebo - Sickle Cell Disease, Sickle Cell Anemia
Phase 2TerminatedHemaQuest Pharmaceuticals Inc.772012-07-012015-03-18
A Study of HQK-1001 in Patients With Sickle Cell Disease
HQK-1001 - Sickle Cell Disease, Sickle Cell Anemia
Phase 2CompletedHemaQuest Pharmaceuticals Inc.522011-04-012013-06-19

Narrower conditions

Anemia, Sickle Cell (4)  ·  Hemoglobin SC Disease (1)

Broader conditions

Anemia (4)  ·  Anemia, Hemolytic (4)  ·  Anemia, Hemolytic, Congenital (4)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4)  ·  Genetic Diseases, Inborn (4)  ·  Hematologic Diseases (4)  ·  Hemic and Lymphatic Diseases (4)  ·  Hemoglobinopathies (4)

Interventions

2,2-dimethylbutyric acid (2)

Sponsors

HemaQuest Pharmaceuticals Inc. (2)  ·  Centre Hospitalier Universitaire de Saint Etienne (1)  ·  University of Regensburg (1)

Countries

Canada (2)  ·  Egypt (2)  ·  Jamaica (2)  ·  Lebanon (2)  ·  United States (2)  ·  Austria (1)  ·  France (1)  ·  Germany (1)

Top investigators

Richard Ghalie, MD, MBA (2)  ·  Selim Corbacioglu, MD (1)

Results publications

PMID 23828223, PMID 24677033, PMID 30389037, PMID 31742587, PMID 32681734