Gaucher Disease: Clinical Trials

1 trial for Gaucher Disease, newest first

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1 unknown. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Unknown 1
Phase 21Unknown 1

Follow Gaucher Disease: new trials by email Literature Review of Gaucher Disease trials Research Report on Gaucher Disease

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase 1/2 Study of CAN103 in Subjects With Gaucher Disease
Low-dose CAN103, High-dose CAN103 - Gaucher Disease, Type 1, Gaucher Disease, Type 3
Phase 1 / Phase 2UnknownCANbridge (Suzhou) Bio-pharma Co., Ltd.402022-07-112022-07-27

Broader conditions

Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Lipidoses (1)  ·  Lysosomal Storage Diseases (1)  ·  Lysosomal Storage Diseases, Nervous System (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nervous System Diseases (1)  ·  Nutritional and Metabolic Diseases (1)

Sponsors

CANbridge (Suzhou) Bio-pharma Co., Ltd. (1)

Countries

China (1)

Top investigators

Bing Han, MD (1)