1 completed, 1 withdrawn. 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
Follow Gamma-sarcoglycanopathy: new trials by email Literature Review of Gamma-sarcoglycanopathy trials Research Report on Gamma-sarcoglycanopathy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Natural History Study in Patients With LGMDR5/2c Gamma-sarcoglycanopathy | Withdrawn | Atamyo Therapeutics | 2025-01-10 | 2025-10-06 | ||
| Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C AAV1-gamma-sarcoglycan vector injection - Limb Girdle Muscular Dystrophy Type 2C, Gamma-sarcoglycanopathy | Phase 1 | Completed | Genethon | 9 | 2006-11-01 | 2011-04-29 |
Limb-girdle muscular dystrophy, type 2C (2) · Neuromuscular Diseases (1) · Rare Diseases (1)
Disease Attributes (1) · Nervous System Diseases (1) · Pathologic Processes (1) · Pathological Conditions, Signs and Symptoms (1)
Atamyo Therapeutics (1) · Genethon (1)
France (2) · Tunisia (1)