1 recruiting. 1 Not applicable.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 1 | Recruiting 1 |
Follow ARG1 Deficiency: new trials by email Literature Review of ARG1 Deficiency trials Research Report on ARG1 Deficiency
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Evaluation of the Safety of Loargys Arginine Test System in Loargys-treated Patients Loargys Arginine Test System - ARG1 Deficiency | Not applicable | Recruiting | Immedica Pharma US Inc | 100 | 2026-04-17 | 2026-05-07 |
Hyperargininemia (1)
Amino Acid Metabolism, Inborn Errors (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Nervous System Diseases (1) · Nutritional and Metabolic Diseases (1) · Urea Cycle Disorders, Inborn (1)
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