ARG1 Deficiency: Clinical Trials

1 trial for ARG1 Deficiency, newest first

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1 recruiting. 1 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable1Recruiting 1

Follow ARG1 Deficiency: new trials by email Literature Review of ARG1 Deficiency trials Research Report on ARG1 Deficiency

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Evaluation of the Safety of Loargys Arginine Test System in Loargys-treated Patients
Loargys Arginine Test System - ARG1 Deficiency
Not applicableRecruitingImmedica Pharma US Inc1002026-04-172026-05-07

Narrower conditions

Hyperargininemia (1)

Broader conditions

Amino Acid Metabolism, Inborn Errors (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nervous System Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Urea Cycle Disorders, Inborn (1)

Sponsors

Immedica Pharma US Inc (1)

Countries

United States (1)

Top investigators

Mattias Rudebeck, PhD (1)