1 enrolling by invitation. 1 Phase 4.
| Phase | Trials | Status |
|---|---|---|
| Phase 4 | 1 | Enrolling by invitation 1 |
Follow Anemia: new trials by email Literature Review of Anemia trials Research Report on Anemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study to Provide Access to Mitapivat for Participants Who Previously Participated in an Agios-Sponsored Mitapivat Study Mitapivat - Pyruvate Kinase Deficiency, Anemia, Hemolytic | Phase 4 | Enrolling by invitation | Agios Pharmaceuticals, Inc. | 55 | 2023-07-06 | 2026-10-28 |
Anemia, Hemolytic (1) · Anemia, Sickle Cell (1) · Pyruvate Kinase Deficiency of Red Cells (1) · Thalassemia (1)
Anemia, Hemolytic, Congenital (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Hematologic Diseases (1) · Hemic and Lymphatic Diseases (1) · Hemoglobinopathies (1)
mitapivat (1)
Agios Pharmaceuticals, Inc. (1)
Belgium (1) · Brazil (1) · Canada (1) · France (1) · Israel (1) · Japan (1) · Turkey (Türkiye) (1) · United Kingdom (1)