3 completed. 3 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 3 | Completed 3 |
Follow alpha-Mannosidosis: new trials by email Literature Review of alpha-Mannosidosis trials Research Report on alpha-Mannosidosis
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Trial on Safety and Efficacy of Velmanase Alfa Treatment in Pediatric Patients With Alpha-Mannosidosis Velmanase Alfa (e.g. Lamazym) - Alpha-Mannosidosis | Phase 2 | Completed | Chiesi Farmaceutici S.p.A. | 5 | 2016-12-01 | 2021-10-26 |
| Long-term Efficacy and Safety of Lamazym for the Treatment of Patients With Alpha-Mannosidosis Lamazym - Alpha-Mannosidosis | Phase 2 | Completed | Zymenex A/S | 10 | 2012-01-01 | 2017-03-29 |
| Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders Campath-1H, Cyclophosphamide, Busulfan - Mucopolysaccharidosis, Hurler Syndrome | Phase 2 | Completed | Masonic Cancer Center, University of Minnesota | 46 | 2009-12-01 | 2018-02-05 |
Adrenoleukodystrophy (1) · Aspartylglucosaminuria (1) · Fucosidosis (1) · Leukodystrophy, Globoid Cell (1) · Leukodystrophy, Metachromatic (1) · Mucopolysaccharidoses (1) · Mucopolysaccharidosis I (1) · Mucopolysaccharidosis II (1) · Mucopolysaccharidosis VI (1) · Mucopolysaccharidosis VII (1) · Peroxisomal Disorders (1) · Sphingolipidoses (1)
Carbohydrate Metabolism, Inborn Errors (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Genetic Diseases, Inborn (3) · Lysosomal Storage Diseases (3) · Mannosidase Deficiency Diseases (3) · Metabolic Diseases (3) · Metabolism, Inborn Errors (3) · Nutritional and Metabolic Diseases (3) · Adrenal Gland Diseases (1) · Adrenal Insufficiency (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Connective Tissue Diseases (1)
Alemtuzumab (1) · Busulfan (1) · Cyclophosphamide (1) · Cyclosporine (1) · Mycophenolic Acid (1) · Stem Cell Transplantation (1)
Chiesi Farmaceutici S.p.A. (1) · Masonic Cancer Center, University of Minnesota (1) · Zymenex A/S (1)
Denmark (2) · Austria (1) · Belgium (1) · France (1) · Germany (1) · Italy (1) · Spain (1) · United Kingdom (1) · United States (1)
Allan M Lund, MD (1) · Jens Fogh (1) · Paul Orchard, MD (1)
2016 (1)