4 unknown. 4 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 4 | Unknown 4 |
Follow Abnormalities, Multiple: new trials by email Literature Review of Abnormalities, Multiple trials Research Report on Abnormalities, Multiple
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| BF844 Safety and Pharmacokinetic Study in Healthy Volunteers BF844 - Usher Syndrome Type 3 | Phase 1 | Unknown | EyeXCel Pty. Ltd. | 76 | 2024-09-09 | 2024-09-19 |
| A Study of BPI-452080 in Subjects With Solid Tumors BPI-452080 - Solid Tumor, Renal Cell Carcinoma | Phase 1 | Unknown | Betta Pharmaceuticals Co., Ltd. | 87 | 2023-04-28 | 2023-05-06 |
| Deep Brain Stimulation for the Treatment of Obesity in Patients With Prader-Willi Syndrome Deep Brain Stimulation - Prader-Willi Syndrome | Phase 1 | Unknown | University of Sao Paulo General Hospital | 6 | 2014-10-01 | 2015-12-16 |
| Gene Therapy for Netherton Syndrome One 20cm2/10cm2 autologous skin sheet graft - Netherton Syndrome | Phase 1 | Unknown | Great Ormond Street Hospital for Children NHS Foundation Trust | 5 | 2014-04-01 | 2016-10-19 |
Carcinoma, Renal Cell (1) · Netherton Syndrome (1) · Obesity (1) · Prader-Willi Syndrome (1) · Usher Syndromes (1) · von Hippel-Lindau Disease (1)
Congenital Abnormalities (4) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4) · Genetic Diseases, Inborn (4) · Nervous System Diseases (3) · Neurologic Manifestations (2) · Pathological Conditions, Signs and Symptoms (2) · Signs and Symptoms (2) · Adenocarcinoma (1) · Angiomatosis (1) · Blindness (1) · Body Weight (1) · Carcinoma (1) · Cardiovascular Diseases (1) · Chromosome Disorders (1)
Betta Pharmaceuticals Co., Ltd. (1) · EyeXCel Pty. Ltd. (1) · Great Ormond Street Hospital for Children NHS Foundation Trust (1) · University of Sao Paulo General Hospital (1)
Australia (1) · Brazil (1) · China (1) · United Kingdom (1)
Benedict Tan, MBBS, FRACP (1) · Dingwei Ye, Ph.D (1) · Durval Damiani (1) · Jemima Mellerio, Dr (1) · Jian Zhang, Ph.D (1)