Solid Biosciences Inc.: Clinical Trials

7 trials sponsored by Solid Biosciences Inc., newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

4 recruiting, 2 completed, 1 active not recruiting. 4 Phase 1, 2 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 14Recruiting 3, Active not recruiting 1
Phase 22Active not recruiting 1, Recruiting 1
Phase 31Recruiting 1

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Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study of SGT-501 Gene Therapy in Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT)
SGT-501 - Catecholaminergic Polymorphic Ventricular Tachycardia
Phase 1RecruitingSolid Biosciences Inc.182026-02-232026-10-26
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
SGT-003, Placebo - Duchenne Muscular Dystrophy
Phase 3RecruitingSolid Biosciences Inc.802025-10-222026-09-28
A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
SGT-212 - Friedreich's Ataxia (FA)
Phase 1RecruitingSolid Biosciences Inc.102025-10-222026-11-06
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
SGT-003 - Duchenne Muscular Dystrophy
Phase 1 / Phase 2RecruitingSolid Biosciences Inc.602024-05-062026-07-08
Evaluation of Home Based Assessments on Participants With DMD
Wearable Device, Duchenne Video Assessment (DVA) - Duchenne Muscular Dystrophy
CompletedSolid Biosciences Inc.172022-10-132023-08-14
Your Voice; Impact of Duchenne Muscular Dystrophy (DMD) on the Lives of Families
Duchenne Muscular Dystrophy, Burden, Dependency
CompletedJett Foundation, Inc.602018-09-202019-04-01
Microdystrophin Gene Transfer Study in Adolescents and Children With DMD
SGT-001 - Duchenne Muscular Dystrophy
Phase 1 / Phase 2Active not recruitingSolid Biosciences Inc.122017-12-062026-10-15

Conditions studied

Muscular Dystrophy, Duchenne (5)  ·  Rare Diseases (2)  ·  Ataxia (1)  ·  Friedreich Ataxia (1)  ·  Movement Disorders (1)  ·  Muscular Dystrophies (1)  ·  Polymorphic Catecholaminergic Ventricular Tachycardia (1)

Interventions

Wearable Electronic Devices (1)

Countries

United States (7)  ·  Canada (3)  ·  Australia (1)  ·  Italy (1)  ·  United Kingdom (1)

Top investigators

Carl A Morris, PhD (1)  ·  Christine McSherry, R.N. (1)

Results publications

PMID 38229112

NIH funding

2025 (1)