Encoded Therapeutics: Clinical Trials

3 trials sponsored by Encoded Therapeutics, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 active not recruiting, 1 recruiting. 3 Phase 1, 3 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 13Active not recruiting 2, Recruiting 1
Phase 23Active not recruiting 2, Recruiting 1

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Trials (filtered) newest first · largest first

All 3 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome
ETX101 - Dravet Syndrome
Phase 1 / Phase 2RecruitingEncoded Therapeutics1132024-05-142026-10-23
A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome
ETX101 - Dravet Syndrome
Phase 1 / Phase 2Active not recruitingEncoded Therapeutics52024-05-092026-06-08
A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome (Australia Only)
ETX101 - Dravet Syndrome
Phase 1 / Phase 2Active not recruitingEncoded Therapeutics42024-02-282025-11-14

Conditions studied

Epilepsies, Myoclonic (3)  ·  Generalized Epilepsy With Febrile Seizures Plus, Type 2 (2)

Countries

Australia (2)  ·  United Kingdom (2)  ·  United States (1)

Top investigators

Salvador Rico, M.D., Ph.D (2)  ·  Salvador Rico, M.D., Ph. D (1)