3 recruiting, 2 active not recruiting, 1 terminated, 1 unknown. 3 Phase 1, 3 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 3 | Active not recruiting 2, Recruiting 1 |
| Phase 2 | 3 | Active not recruiting 2, Recruiting 1 |
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Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Longitudinal Study of Phenotypic and Developmental Severity in Patients With Dravet Syndrome With SCN1A Gene Mutation Dravet Syndrome | Recruiting | Assistance Publique - Hôpitaux de Paris | 50 | 2025-09-15 | 2026-02-03 | |
| A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome ETX101 - Dravet Syndrome | Phase 1 / Phase 2 | Recruiting | Encoded Therapeutics | 113 | 2024-05-14 | 2026-10-23 |
| A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome ETX101 - Dravet Syndrome | Phase 1 / Phase 2 | Active not recruiting | Encoded Therapeutics | 5 | 2024-05-09 | 2026-06-08 |
| A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome (Australia Only) ETX101 - Dravet Syndrome | Phase 1 / Phase 2 | Active not recruiting | Encoded Therapeutics | 4 | 2024-02-28 | 2025-11-14 |
| GABA Biomarkers in Dravet Syndrome GABA Blood Level - Dravet Syndrome | Recruiting | Cook Children's Health Care System | 36 | 2022-09-08 | 2022-12-14 | |
| Natural History Study of Infants and Children With Developmental and Epileptic Encephalopathies No Intervention - Dravet Syndrome | Terminated | Encoded Therapeutics | 58 | 2021-01-18 | 2023-06-12 | |
| Transcranial Magnetic Stimulation to Measure Cortical Excitability in Dravet Syndrome Transcranial Magnetic Stimulation (TMS), Electroencephalogram (EEG) - Dravet Syndrome | Unknown | Boston Children's Hospital | 6 | 2020-11-02 | 2022-03-22 |
Epilepsies, Myoclonic (7) · Epilepsy (2) · Generalized Epilepsy With Febrile Seizures Plus, Type 2 (2)
Electroencephalography (1) · Transcranial Magnetic Stimulation (1)
United States (4) · Australia (3) · United Kingdom (3) · France (1) · Spain (1)
Salvador Rico, M.D., Ph.D (3) · Alexander Rotenberg, MD, PhD (1) · Christos Papadelis, PhD (1) · Salvador Rico, M.D., Ph. D (1)