tofersen: Clinical Trials

1 trial of tofersen, newest first

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1 recruiting. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Recruiting 1

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Trials (filtered) newest first · largest first

All 1 trial

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TrialPhaseStatusSponsorEnrollmentStartUpdated
Tofersen in Non-SOD1 ALS
Tofersen - ALS (Amyotrophic Lateral Sclerosis)
Phase 2RecruitingWashington University School of Medicine302025-12-292026-06-25

Conditions studied

Amyotrophic Lateral Sclerosis (1)

Sponsors

Washington University School of Medicine (1)

Countries

United States (1)