2 completed. 2 Phase 3, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 2 | Completed 2 |
| Phase 2 | 1 | Completed 1 |
Follow Sebelipase alfa: new trials by email Literature Review of Sebelipase alfa trials Research Report on Sebelipase alfa
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Acid Lipase Replacement Investigating Safety and Efficacy (ARISE) in Participants With Lysosomal Acid Lipase Deficiency Sebelipase Alfa, Placebo - Lysosomal Acid Lipase Deficiency | Phase 3 | Completed | Alexion Pharmaceuticals, Inc. | 66 | 2013-01-22 | 2020-12-29 |
| Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of Sebelipase Alfa in Children With Growth Failure Due to Lysosomal Acid Lipase Deficiency Sebelipase alfa (SBC-102) - Lysosomal Acid Lipase Deficiency, Wolman Disease | Phase 2 / Phase 3 | Completed | Alexion Pharmaceuticals, Inc. | 9 | 2011-05-04 | 2019-01-30 |
Cholesterol Ester Storage Disease (2) · Wolman Disease (2) · Chanarin-Dorfman Syndrome (1) · Cirrhosis, Cryptogenic (1) · Liver Diseases, Alcoholic (1) · Lysosomal Storage Diseases (1) · Niemann-Pick Diseases (1) · Non-alcoholic Fatty Liver Disease (1)
Alexion Pharmaceuticals, Inc. (2)
France (2) · United Kingdom (2) · United States (2) · Argentina (1) · Australia (1) · Croatia (1) · Czechia (1) · Egypt (1) · Germany (1) · Ireland (1) · Italy (1) · Japan (1) · Mexico (1) · Poland (1) · Russia (1)
Florian Abel, MD (1)