1 completed, 1 recruiting. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
| Phase 2 | 1 | Recruiting 1 |
Follow RP-A501: new trials by email Literature Review of RP-A501 trials Research Report on RP-A501
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease RP-A501 - Danon Disease | Phase 2 | Recruiting | Rocket Pharmaceuticals Inc. | 18 | 2023-09-05 | 2026-10-06 |
| Gene Therapy for Male Patients With Danon Disease (DD) Using RP-A501; AAV9.LAMP2B RP-A501 - Danon Disease | Phase 1 | Completed | Rocket Pharmaceuticals Inc. | 7 | 2019-04-17 | 2026-10-06 |
Cardiomyopathy, Hypertrophic (2) · Glycogen Storage Disease Type IIb (2) · Cardiomyopathies (1) · Hypertrophy, Left Ventricular (1) · Lysosomal Storage Diseases (1)
Rocket Pharmaceuticals Inc. (2)
United States (2) · Germany (1) · Italy (1) · United Kingdom (1)
Barry Greenberg, MD (2) · Joseph Rossano, MD (2) · Matthew Taylor, MD, PhD (1)