Phenylbutyrates: Clinical Trials

2 trials of Phenylbutyrates, newest first

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2 completed. 2 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 22Completed 2
Phase 31Completed 1

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Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phenylbutyrate Therapy for Maple Syrup Urine Disease
Phenylbutyrate, Placebo powder - Maple Syrup Urine Disease
Phase 2 / Phase 3CompletedBrendan Lee202013-02-012019-03-19
Phenylbutyrate to Treat Children With Progressive or Recurrent Brain Tumors
Phenylbutyrate - Brain Tumor
Phase 2CompletedNational Cancer Institute (NCI)1202000-11-012008-03-04

Conditions studied

Brain Neoplasms (1)  ·  Maple Syrup Urine Disease (1)

Sponsors

Brendan Lee (1)  ·  National Cancer Institute (NCI) (1)

Countries

United States (2)

Top investigators

Brendan Lee, M.D., Ph.D. (1)