Cemdisiran: Clinical Trials

6 trials of Cemdisiran, newest first

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3 recruiting, 2 active not recruiting, 1 terminated. 6 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 36Recruiting 3, Active not recruiting 2, Terminated 1

Follow Cemdisiran: new trials by email Literature Review of Cemdisiran trials Research Report on Cemdisiran

Trials (filtered) newest first · largest first

All 6 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study to Evaluate How Pozelimab + Cemdisiran Combination Therapy Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Whose Current Treatment is Not Working Efficiently
Pozelimab, Cemdisiran - Paroxysmal Nocturnal Hemoglobinuria
Phase 3RecruitingRegeneron Pharmaceuticals352026-06-112026-08-05
A Study Investigating Subcutaneously Administered Pozelimab in Combination With Cemdisiran or Cemdisiran Alone in Adult Participants With Geographic Atrophy
Pozelimab, Cemdisiran, Placebo - Age-related Macular Degeneration (AMD), Geographic Atrophy (GA)
Phase 3RecruitingRegeneron Pharmaceuticals9752024-10-302026-10-13
A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works
Pozelimab, Cemdisiran - Paroxysmal Nocturnal Hemoglobinuria
Phase 3RecruitingRegeneron Pharmaceuticals2022023-03-072026-09-28
Efficacy and Safety of the Combination of Pozelimab and Cemdisiran Versus Continued Eculizumab or Ravulizumab Treatment in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria
Cemdisiran, Eculizumab, Pozelimab - Paroxysmal Nocturnal Hemoglobinuria
Phase 3TerminatedRegeneron Pharmaceuticals32022-10-062025-04-08
A Study to Evaluate How Safe Pozelimab + Cemdisiran Combination Therapy is and How Well it Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Who Have Not Recently Received or Have Not Received Complement Inhibitor Treatment
Ravulizumab, Pozelimab, Cemdisiran - Paroxysmal Nocturnal Hemoglobinuria
Phase 3Active not recruitingRegeneron Pharmaceuticals2022022-08-012026-04-30
A Study to Test How Safe Pozelimab and Cemdisiran Combination Therapy and Cemdisiran Alone Are and How Well They Work in Adult Patients With Generalized Myasthenia Gravis
Pozelimab + Cemdisiran, Cemdisiran, Placebo - Generalized Myasthenia Gravis
Phase 3Active not recruitingRegeneron Pharmaceuticals2882021-12-142026-10-28

Conditions studied

Hemoglobinuria, Paroxysmal (4)  ·  Geographic Atrophy (1)  ·  Macular Degeneration (1)  ·  Myasthenia Gravis (1)

Sponsors

Regeneron Pharmaceuticals (6)

Countries

Canada (5)  ·  Italy (5)  ·  Poland (5)  ·  Spain (5)  ·  Brazil (4)  ·  South Korea (4)  ·  Turkey (Türkiye) (4)  ·  United Kingdom (4)  ·  United States (4)  ·  Hungary (3)  ·  India (3)  ·  Japan (3)  ·  Taiwan (3)  ·  China (2)  ·  Colombia (2)

Results publications

PMID 42030965

NIH funding

2023 (4)