ataluren: Clinical Trials

5 trials of ataluren, newest first

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5 terminated. 5 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 25Terminated 5

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Trials (filtered) newest first · largest first

All 5 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Ataluren for Nonsense Mutation Methylmalonic Acidemia
Ataluren - Amino Acid Metabolism, Inborn Errors
Phase 2TerminatedPTC Therapeutics112010-07-192020-07-07
Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)
Ataluren, Chronic Corticosteroid Therapy - Duchenne Muscular Dystrophy, Becker Muscular Dystrophy
Phase 2TerminatedPTC Therapeutics62010-01-132020-07-29
Study of Ataluren (PTC124) in Hemophilia A and B
Ataluren - Hemophilia A, Hemophilia B
Phase 2TerminatedPTC Therapeutics132009-10-142020-06-16
Phase 2B Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD)
Ataluren - Duchenne Muscular Dystrophy, Becker Muscular Dystrophy
Phase 2TerminatedPTC Therapeutics1732009-01-312020-07-15
Phase 2a Extension Study of Ataluren (PTC124) in Duchenne Muscular Dystrophy (DMD)
Ataluren - Duchenne Muscular Dystrophy
Phase 2TerminatedPTC Therapeutics362008-08-132020-10-29

Conditions studied

Muscular Dystrophy, Duchenne (3)  ·  Amino Acid Metabolism, Inborn Errors (1)  ·  Hemophilia A (1)  ·  Hemophilia B (1)

Sponsors

PTC Therapeutics (5)

Countries

United States (4)  ·  France (3)  ·  Italy (3)  ·  United Kingdom (3)  ·  Belgium (2)  ·  Canada (2)  ·  Germany (2)  ·  Australia (1)  ·  Israel (1)  ·  Spain (1)  ·  Sweden (1)  ·  Switzerland (1)

Top investigators

Jay Barth, MD (2)  ·  Leone Atkinson (1)  ·  Leone Atkinson, M.D., Ph.D. (1)  ·  Leone Atkinson, MD, PhD (1)

NIH funding

2009 (1)