5 terminated. 5 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 5 | Terminated 5 |
Follow ataluren: new trials by email Literature Review of ataluren trials Research Report on ataluren
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Ataluren for Nonsense Mutation Methylmalonic Acidemia Ataluren - Amino Acid Metabolism, Inborn Errors | Phase 2 | Terminated | PTC Therapeutics | 11 | 2010-07-19 | 2020-07-07 |
| Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD) Ataluren, Chronic Corticosteroid Therapy - Duchenne Muscular Dystrophy, Becker Muscular Dystrophy | Phase 2 | Terminated | PTC Therapeutics | 6 | 2010-01-13 | 2020-07-29 |
| Study of Ataluren (PTC124) in Hemophilia A and B Ataluren - Hemophilia A, Hemophilia B | Phase 2 | Terminated | PTC Therapeutics | 13 | 2009-10-14 | 2020-06-16 |
| Phase 2B Extension Study of Ataluren (PTC124) in Duchenne/Becker Muscular Dystrophy (DMD/BMD) Ataluren - Duchenne Muscular Dystrophy, Becker Muscular Dystrophy | Phase 2 | Terminated | PTC Therapeutics | 173 | 2009-01-31 | 2020-07-15 |
| Phase 2a Extension Study of Ataluren (PTC124) in Duchenne Muscular Dystrophy (DMD) Ataluren - Duchenne Muscular Dystrophy | Phase 2 | Terminated | PTC Therapeutics | 36 | 2008-08-13 | 2020-10-29 |
Muscular Dystrophy, Duchenne (3) · Amino Acid Metabolism, Inborn Errors (1) · Hemophilia A (1) · Hemophilia B (1)
PTC Therapeutics (5)
United States (4) · France (3) · Italy (3) · United Kingdom (3) · Belgium (2) · Canada (2) · Germany (2) · Australia (1) · Israel (1) · Spain (1) · Sweden (1) · Switzerland (1)
Jay Barth, MD (2) · Leone Atkinson (1) · Leone Atkinson, M.D., Ph.D. (1) · Leone Atkinson, MD, PhD (1)
2009 (1)