Xeroderma Pigmentosum, Complementation Group F: Clinical Trials

1 trial for Xeroderma Pigmentosum, Complementation Group F, newest first

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1 recruiting. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Recruiting 1
Phase 21Recruiting 1

Follow Xeroderma Pigmentosum, Complementation Group F: new trials by email Literature Review of Xeroderma Pigmentosum, Complementation Group F trials Research Report on Xeroderma Pigmentosum, Complementation Group F

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety and Efficacy Study of Transplantation of Autologous CD34+ Cells Transduced With the G2ARTE Lentiviral Vector Expressing the DCLRE1C cDNA in Artemis (DCLRE1C) Deficient Severe Combined Immunodeficiency Patients (ARTEGENE)
ARTEGENE drug product - Artemis (DCLRE1C ) Deficient Severe Combined Immunodeficiency
Phase 1 / Phase 2RecruitingAssistance Publique - Hôpitaux de Paris72023-07-192026-03-27

Narrower conditions

Severe Combined Immunodeficiency (1)  ·  Severe combined immunodeficiency with sensitivity to ionizing radiation (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  DNA Repair-Deficiency Disorders (1)  ·  Genetic Diseases, Inborn (1)  ·  Immune System Diseases (1)  ·  Immunologic Deficiency Syndromes (1)  ·  Infant, Newborn, Diseases (1)  ·  Metabolic Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Primary Immunodeficiency Diseases (1)

Sponsors

Assistance Publique - Hôpitaux de Paris (1)

Countries

France (1)

Top investigators

Chantal Lagresle-Peyrou, MD (1)

NIH funding

2019 (1)