2 completed. 2 Phase 1, 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Completed 2 |
| Phase 2 | 2 | Completed 2 |
Follow VLCAD deficiency: new trials by email Literature Review of VLCAD deficiency trials Research Report on VLCAD deficiency
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study to Evaluate the Safety and Therapeutic Effects of Transplantation of MNV-BM-BLD in Pediatric Patients With Pearson Syndrome CD34+ cells enriched with MNV-BLD - Mitochondrial Diseases, Pearson Syndrome | Phase 1 / Phase 2 | Completed | Minovia Therapeutics Ltd. | 7 | 2019-02-13 | 2021-08-31 |
| High Protein Diet in Patients With Long-chain Fatty Acid Oxidation Disorders Diet counseling - Very Long-chain Acyl-CoA Dehydrogenase Deficiency, Trifunctional Protein Deficiency | Phase 1 / Phase 2 | Completed | Oregon Health and Science University | 13 | 2006-01-01 | 2020-04-29 |
Carnitine palmitoyl transferase 2 deficiency (1) · Mitochondrial Diseases (1) · Rare Diseases (1) · Trifunctional Protein Deficiency With Myopathy And Neuropathy (1)
Disease Attributes (1) · Metabolic Diseases (1) · Nutritional and Metabolic Diseases (1) · Pathologic Processes (1) · Pathological Conditions, Signs and Symptoms (1)
Diet, Fat-Restricted (1) · Diet, High-Protein (1) · Diet, High-Protein Low-Carbohydrate (1)
Minovia Therapeutics Ltd. (1) · Oregon Health and Science University (1)
Israel (1)