VEXAS: Clinical Trials

1 trial for VEXAS, newest first

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1 recruiting. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Recruiting 1

Follow VEXAS: new trials by email Literature Review of VEXAS trials Research Report on VEXAS

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study to Assess the Effectiveness and Safety of Pacritinib in Patients With VEXAS Syndrome (PAXIS)
Pacritinib, Placebo - VEXAS, VEXAS Syndrome
Phase 2RecruitingSwedish Orphan Biovitrum1562025-05-282026-10-16

Narrower conditions

Hematologic Neoplasms (1)  ·  Myelodysplastic Syndromes (1)  ·  VEXAS syndrome (1)

Broader conditions

Bone Marrow Diseases (1)  ·  Hematologic Diseases (1)  ·  Hemic and Lymphatic Diseases (1)  ·  Neoplasms (1)  ·  Neoplasms by Site (1)

Interventions

11-(2-pyrrolidin-1-ylethoxy)-14,19-dioxa-5,7,26-triazatetracyclo(19.3.1.1(2,6).1(8,12))heptacosa-1(25),2(26),3,5,8,10,12(27),16,21,23-decaene (1)

Sponsors

Swedish Orphan Biovitrum (1)

Countries

Canada (1)  ·  France (1)  ·  Germany (1)  ·  Italy (1)  ·  Japan (1)  ·  Spain (1)  ·  United Kingdom (1)  ·  United States (1)

Results publications

PMID 41753113