Severe Combined Immunodeficiency, X Linked: Clinical Trials

1 trial for Severe Combined Immunodeficiency, X Linked, newest first

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1 recruiting. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Recruiting 1
Phase 21Recruiting 1

Follow Severe Combined Immunodeficiency, X Linked: new trials by email Literature Review of Severe Combined Immunodeficiency, X Linked trials Research Report on Severe Combined Immunodeficiency, X Linked

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase I/II Trial of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan Conditioning
autologous CD34+ cell transduced with G2SCID vector - Severe Combined Immunodeficiency, X Linked, Gene Therapy
Phase 1 / Phase 2RecruitingDavid Williams122018-02-262025-12-11

Narrower conditions

X-Linked Combined Immunodeficiency Diseases (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Immune System Diseases (1)  ·  Immunologic Deficiency Syndromes (1)  ·  Infant, Newborn, Diseases (1)  ·  Primary Immunodeficiency Diseases (1)  ·  Severe Combined Immunodeficiency (1)

Sponsors

David Williams (1)

Countries

United States (1)

Top investigators

Sung-Yun Pai, MD (1)