Purine Nucleoside Phosphorylase Deficiency: Clinical Trials

1 trial for Purine Nucleoside Phosphorylase Deficiency, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 completed. 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1

Follow Purine Nucleoside Phosphorylase Deficiency: new trials by email Literature Review of Purine Nucleoside Phosphorylase Deficiency trials Research Report on Purine Nucleoside Phosphorylase Deficiency

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Total-Body Irradiation Followed By Cyclosporine and Mycophenolate Mofetil in Treating Patients With Severe Combined Immunodeficiency Undergoing Donor Bone Marrow Transplant
Allogeneic Bone Marrow Transplantation, Cyclosporine, Laboratory Biomarker Analysis - Adenosine Deaminase Deficiency, Autosomal Recessive Disorder
Phase 1CompletedFred Hutchinson Cancer Center61997-08-112019-07-29

Narrower conditions

Immune System Diseases (1)  ·  Severe Combined Immunodeficiency (1)  ·  Severe combined immunodeficiency due to adenosine deaminase deficiency (1)  ·  X-Linked Combined Immunodeficiency Diseases (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  DNA Repair-Deficiency Disorders (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Immunologic Deficiency Syndromes (1)  ·  Infant, Newborn, Diseases (1)  ·  Metabolic Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Primary Immunodeficiency Diseases (1)

Interventions

Cyclosporine (1)  ·  Cyclosporins (1)  ·  Mycophenolic Acid (1)  ·  Whole-Body Irradiation (1)

Sponsors

Fred Hutchinson Cancer Center (1)

Countries

United States (1)

Top investigators

Lauri Burroughs (1)

NIH funding

P01HL036444 (1), P30CA015704 (1)