Pseudoxanthoma Elasticum: Clinical Trials

1 trial for Pseudoxanthoma Elasticum, newest first

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1 terminated. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Terminated 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
ADAPT Study: Long-term Safety Study of INZ-701 in Patients With ENPP1 Deficiency and ABCC6 Deficiency
INZ-701 - Gene Mutations, Pseudoxanthoma Elasticum
Phase 2TerminatedInozyme Pharma222024-06-192026-10-19

Narrower conditions

Arterial calcification of infancy (1)

Broader conditions

Cardiovascular Diseases (1)  ·  Congenital Abnormalities (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Connective Tissue Diseases (1)  ·  Genetic Diseases, Inborn (1)  ·  Hematologic Diseases (1)  ·  Hemic and Lymphatic Diseases (1)  ·  Hemorrhagic Disorders (1)  ·  Hemostatic Disorders (1)  ·  Skin Abnormalities (1)  ·  Skin Diseases (1)  ·  Skin Diseases, Genetic (1)  ·  Skin and Connective Tissue Diseases (1)  ·  Vascular Diseases (1)

Sponsors

Inozyme Pharma (1)

Countries

France (1)  ·  Germany (1)  ·  United Kingdom (1)  ·  United States (1)

Top investigators

Kurt Gunter, MD (1)