Propionic Acidemia: Clinical Trials

2 trials for Propionic Acidemia, newest first

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2 recruiting. 2 Phase 1, 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Recruiting 2
Phase 22Recruiting 2

Follow Propionic Acidemia: new trials by email Literature Review of Propionic Acidemia trials Research Report on Propionic Acidemia

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
mRNA-3927 - Propionic Acidemia
Phase 1 / Phase 2RecruitingModernaTX, Inc.502021-11-092026-03-23
Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
mRNA-3927 - Propionic Acidemia
Phase 1 / Phase 2RecruitingModernaTX, Inc.772021-04-152026-01-22

Narrower conditions

Acid-Base Imbalance (2)  ·  Acidosis (2)  ·  Amino Acid Metabolism, Inborn Errors (2)  ·  Genetic Diseases, Inborn (2)  ·  Metabolic Diseases (2)  ·  Metabolism, Inborn Errors (2)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Nutritional and Metabolic Diseases (2)

Sponsors

ModernaTX, Inc. (2)

Countries

Canada (2)  ·  France (2)  ·  Japan (2)  ·  Netherlands (2)  ·  Saudi Arabia (2)  ·  Spain (2)  ·  United Kingdom (2)  ·  United States (2)

Results publications

PMID 36577040