Progeria: Clinical Trials

1 trial for Progeria, newest first

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1 unknown. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Unknown 1

Follow Progeria: new trials by email Literature Review of Progeria trials Research Report on Progeria

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of Zoledronic Acid, Pravastatin, and Lonafarnib for Patients With Progeria
Lonafarnib, Zoledronic Acid, and Pravastatin - Progeria
Phase 2UnknownBoston Children's Hospital852009-08-012023-02-27

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Laminopathies (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

Pravastatin (1)  ·  Zoledronic Acid (1)  ·  lonafarnib (1)

Sponsors

Boston Children's Hospital (1)

Countries

United States (1)

Top investigators

Mark Kieran, MD, PhD (1)

Results publications

PMID 24795390, PMID 27400896, PMID 36507973, PMID 36919608