Progeria: Clinical Trials

1 trial for Progeria, newest first

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1 enrolling by invitation. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Enrolling by invitation 1
Phase 21Enrolling by invitation 1

Follow Progeria: new trials by email Literature Review of Progeria trials Research Report on Progeria

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase I/II Trial of Everolimus in Combination With Lonafarnib in Progeria
Everolimus and lonafarnib - Progeria
Phase 1 / Phase 2Enrolling by invitationBoston Children's Hospital802015-12-012026-04-02

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Laminopathies (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

Everolimus (1)  ·  lonafarnib (1)

Sponsors

Boston Children's Hospital (1)

Countries

United States (1)

Top investigators

Monica Kleinman, M.D. (1)